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Genetic Diseases
Optimal dosing regimen for treating seizures and self-aggressive behavior
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Obstetrics
Analysis of the genetic factors that contribute to the duration of gestation and risk of preterm birth has led to identification of druggable targets to prevent preterm birth.
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Anti-Aging
CASIN significantly increases murine lifespan and epigenetic clock.
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Pulmonology
Rapid and highly effective mucus clearance from airways without active coughing.
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Oncology
Our proprietary inhibitor binds to Vav3 thereby inhibiting the activation of Rac and the estrogen receptor.
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Gene and Cell therapy
Organoids provide an unprecedented opportunity to study human organ development and physiology, and investigate the cause of disease.
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Genetics
Immunology
Complement 5a increases inflammation in Hunter Syndrome
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Pulmonology
Repurposing a phase I/II compound (AURKB inhibitor - barasertib) for idiopathic pulmonary fibrosis therapy.
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Immunology
Human Natural Killer cells expressing chimeric antigen receptor that targets aberrant immune system signaling that is involved in auto-antibody production associated with Systemic Lupus Erythematosus.
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Neurodegenerative Diseases
Restore GCase activity in the brain for Gaucher and Parkinson's